|
09-2022
|
Non-GLP Expression Study in C57BL/6 Mice
Non-GLP Expression Study in C57BL/6 Mice
|
|
07-2022
|
Testing Gene Therapy in Models of Geographic Atrophy
Testing Gene Therapy in Models of Geographic Atrophy
|
|
03-2022
|
Mito-Targeted AAV to Treat Leber Hereditary Optic Neuropathy Caused by ND4 Mutations
Mito-Targeted AAV to Treat Leber Hereditary Optic Neuropathy Caused by ND4 Mutations
|
|
01-2022
|
Translational Gene Therapy for CNGB1 Retinitis Pigmentosa
Translational Gene Therapy for CNGB1 Retinitis Pigmentosa
|
|
12-2021
|
Vitreal delivery of novel AAV vectors for blue cone monochromacy gene therapy
Vitreal delivery of novel AAV vectors for blue cone monochromacy gene therapy
|
|
08-2021
|
Preclinical Validation for ADVM-062 in Knock-Out and C198R Knock-In Missense Mouse Models of BCM
Preclinical Validation for ADVM-062 in Knock-Out and C198R Knock-In Missense Mouse Models of BCM
|
|
08-2021
|
Translational Research for Retinal Degenerative Therapies
Translational Research for Retinal Degenerative Therapies
|
|
03-2021
|
Disease mechanisms of cone opsin mutants and treatment strategies
Disease mechanisms of cone opsin mutants and treatment strategies
|
|
01-2021
|
Purified Recombinant Adeno Associated Virus
Purified Recombinant Adeno Associated Virus
|
|
03-2020
|
Gene Therapy for ABCA4 Stargardt's Disease
Gene Therapy for ABCA4 Stargardt's Disease
|
|
12-2019
|
Dual Vectors for Otoferlin
Dual Vectors for Otoferlin
|
|
11-2019
|
rAAV-CNGB3 Gene Therapy for Achromatopsia: Translational Research Studies
rAAV-CNGB3 Gene Therapy for Achromatopsia: Translational Research Studies
|
|
06-2019
|
Gene Therapy for RHO adRP
Gene Therapy for RHO adRP
|
|
03-2019
|
Toxicology Study of BS01 in Rd1 mice
Toxicology Study of BS01 in Rd1 mice
|
|
12-2018
|
Gene Therapy for LCA1
Gene Therapy for LCA1
|
|
09-2018
|
blue cone monochromancy
blue cone monochromancy
|
|
07-2018
|
Gene Therapy for CEP290 LCA and RPE Dystrophies
Gene Therapy for CEP290 LCA and RPE Dystrophies
|
|
06-2018
|
Gene Therapy for Blue Cone Monochromacy
Gene Therapy for Blue Cone Monochromacy
|
|
02-2018
|
Translational Gene Therapy for Rhodopsin Autosomal Dominant Retinitis Pigmentosa (Module 1)
Translational Gene Therapy for Rhodopsin Autosomal Dominant Retinitis Pigmentosa (Module 1)
|
|
02-2018
|
AAV-Mediated Therapy for Best Vitelliform Macular Dystrophy
AAV-Mediated Therapy for Best Vitelliform Macular Dystrophy
|
|
01-2018
|
Population Coding in the Retina
Population Coding in the Retina
|
|
10-2017
|
XLRP Mouse Toxicology Study
XLRP Mouse Toxicology Study
|
|
05-2017
|
03091205
03091205
|
|
12-2016
|
XIAP gene therapy for the treatment of retinal degeneration: Safety and toxicity studies for translation into the clinic
XIAP gene therapy for the treatment of retinal degeneration: Safety and toxicity studies for translation into the clinic
|
|
10-2016
|
DSR Match Support - Gene Therapy for ABCA4 Stargar
DSR Match Support - Gene Therapy for ABCA4 Stargar
|
|
09-2016
|
Gene therapy using novel cone-targeted adeno-associated vital vectors in the CNGA3 sheep model of achromatopsia
Gene therapy using novel cone-targeted adeno-associated vital vectors in the CNGA3 sheep model of achromatopsia
|
|
08-2016
|
Translational Research for Retinal Degenerative Therapies
Translational Research for Retinal Degenerative Therapies
|
|
07-2016
|
Vision Research Core
Vision Research Core
|
|
06-2016
|
Gene Therapy for LCA1
Gene Therapy for LCA1
|
|
06-2016
|
Module 1: Cone Targeted Gene Therapy
Module 1: Cone Targeted Gene Therapy
|
|
12-2015
|
Translational Research for Retinal Degenerative Therapie
Translational Research for Retinal Degenerative Therapie
|
|
10-2015
|
Validation of a Novel AAV Vector for Targeted Gene Thera
Validation of a Novel AAV Vector for Targeted Gene Thera
|
|
07-2015
|
Clinical Trials of Gene Therapy for Leber Congenital Ama
Clinical Trials of Gene Therapy for Leber Congenital Ama
|
|
05-2015
|
GENE-REPLACMENT THERAPY FOR XLRP DUE TO RPGR MUTATIONS
GENE-REPLACMENT THERAPY FOR XLRP DUE TO RPGR MUTATIONS
|
|
05-2015
|
Gene Therapy for USH3A
Gene Therapy for USH3A
|
|
03-2015
|
Leber Hereditary Optic Neuropathy Gene Therapy Clinical
Leber Hereditary Optic Neuropathy Gene Therapy Clinical
|
|
12-2014
|
Phase 2: Achromotopsia initiative
Phase 2: Achromotopsia initiative
|
|
12-2014
|
RNA Replacement Therapy for ADRP
RNA Replacement Therapy for ADRP
|
|
11-2014
|
Vector Synthesis and toxicity testing (AIM II.1)
Vector Synthesis and toxicity testing (AIM II.1)
|
|
09-2014
|
ACHM Mouse Promoter Selection Study”
ACHM Mouse Promoter Selection Study”
|
|
09-2014
|
Evaluation of rAAV2tYF-CB-hRS1 Tox/BD Drug Product for T
Evaluation of rAAV2tYF-CB-hRS1 Tox/BD Drug Product for T
|
|
09-2014
|
AAV-based Gene Therapy for X-linked Retinoschisis (XLRP)
AAV-based Gene Therapy for X-linked Retinoschisis (XLRP)
|
|
08-2014
|
Development and optimization of a viral gene delivery sy
Development and optimization of a viral gene delivery sy
|
|
04-2014
|
Leber Hereditary Optic Neuropathy: Gene Therapy Module 3
Leber Hereditary Optic Neuropathy: Gene Therapy Module 3
|
|
04-2014
|
Leber Hereditary Optic Neuropathy: Gene Therapy Trial -M
Leber Hereditary Optic Neuropathy: Gene Therapy Trial -M
|
|
01-2014
|
Achromatopsia-Disease mechanisms and Cone-Directed Gene
Achromatopsia-Disease mechanisms and Cone-Directed Gene
|
|
12-2013
|
Gene Therapy for Usher 3A
Gene Therapy for Usher 3A
|
|
12-2013
|
Developing Gene Therapy for Age Related Macular Degenera
Developing Gene Therapy for Age Related Macular Degenera
|
|
12-2013
|
Novel Gene Therapy Approaches for the Treatment
Novel Gene Therapy Approaches for the Treatment
|
|
11-2013
|
Gene Therapy for Blue Cone Monochromacy
Gene Therapy for Blue Cone Monochromacy
|
|
09-2013
|
Novel Gene Therapy Approaches
Novel Gene Therapy Approaches
|
|
07-2013
|
Clinical Trials of Gene Therapy for Leber Congenital Ama
Clinical Trials of Gene Therapy for Leber Congenital Ama
|
|
03-2013
|
Reduction of Corneal Scarring
Reduction of Corneal Scarring
|
|
03-2013
|
Leber Hereditary Optic neuropathy: Gene Therapy Trial
Leber Hereditary Optic neuropathy: Gene Therapy Trial
|
|
08-2012
|
Experimental Optic Neuritis: A Gene Therapy Trial
Experimental Optic Neuritis: A Gene Therapy Trial
|
|
08-2012
|
Modification of AdenoAssociated Virus to deliver DNA dir
Modification of AdenoAssociated Virus to deliver DNA dir
|
|
08-2012
|
Translational Rsch for Retinal Degeneration Therapies
Translational Rsch for Retinal Degeneration Therapies
|
|
08-2012
|
Gene Therapy for Cone Deficits the RPGR form of X-linked
Gene Therapy for Cone Deficits the RPGR form of X-linked
|
|
08-2012
|
RDS Mutations: Gene Thearpy for ADRP, Macular Degenerati
RDS Mutations: Gene Thearpy for ADRP, Macular Degenerati
|
|
07-2012
|
Clinical Trials of Gene Therapy for Leber Congenital Ama
Clinical Trials of Gene Therapy for Leber Congenital Ama
|
|
06-2012
|
Screening of cone targeting promoters for AAV mediated A
Screening of cone targeting promoters for AAV mediated A
|
|
06-2012
|
MY07A Gene Therapy for Usher 1B
MY07A Gene Therapy for Usher 1B
|
|
06-2012
|
Gene Therapies for Dominant Stargardt s Disease GCI LCA
Gene Therapies for Dominant Stargardt s Disease GCI LCA
|
|
06-2012
|
Module V - Cone Targeted Gene Therapy
Module V - Cone Targeted Gene Therapy
|
|
05-2012
|
Usher 3A
Usher 3A
|
|
04-2012
|
Leber Hereditary Optic Neuropathy: Gene Ther. Trial Mod3
Leber Hereditary Optic Neuropathy: Gene Ther. Trial Mod3
|
|
04-2012
|
Leber Hereditary Optic Neuropathy:Gene Ther. Trial -Mod2
Leber Hereditary Optic Neuropathy:Gene Ther. Trial -Mod2
|
|
04-2012
|
Module 3 Leber Hereditary Optic neuropathy: Gene Therapy
Module 3 Leber Hereditary Optic neuropathy: Gene Therapy
|
|
01-2012
|
Achromatopsia-Disease Mechanisms and Cone-Directed Gene
Achromatopsia-Disease Mechanisms and Cone-Directed Gene
|
|
12-2011
|
Gene Therapy for Usher 1B
Gene Therapy for Usher 1B
|
|
09-2011
|
AGTC funded Translational Studies
AGTC funded Translational Studies
|
|
08-2011
|
Alcon Research program
Alcon Research program
|
|
07-2011
|
Module I Clinical Trials of Gene Therapy for Leber Conge
Module I Clinical Trials of Gene Therapy for Leber Conge
|
|
07-2011
|
Gene Therapy for X-Linked Juvenile Retinoschisis
Gene Therapy for X-Linked Juvenile Retinoschisis
|
|
07-2011
|
Retinal Gene Delivery by AAV
Retinal Gene Delivery by AAV
|
|
05-2011
|
MERTK Gene Therapy for Retinal Degeneration
MERTK Gene Therapy for Retinal Degeneration
|
|
04-2011
|
Leber Hereditary Optic Neuropathy-Module 2 Year 3
Leber Hereditary Optic Neuropathy-Module 2 Year 3
|
|
04-2011
|
Leber Hereditary Optic Neuropathy-Module 3 Year 3
Leber Hereditary Optic Neuropathy-Module 3 Year 3
|
|
03-2011
|
Vision Research Core
Vision Research Core
|
|
01-2011
|
Alcon Misc. Donors
Alcon Misc. Donors
|
|
11-2010
|
MERTK Gene Therapy for Retinal Degeneration
MERTK Gene Therapy for Retinal Degeneration
|
|
10-2010
|
Retinogeographic Distribution of Secreted Retinoschisin
Retinogeographic Distribution of Secreted Retinoschisin
|
|
07-2010
|
Clinical Trials of Gene Therapy for Leber Congenital Ama
Clinical Trials of Gene Therapy for Leber Congenital Ama
|
|
07-2010
|
rAAV5-hCNGB3 Gene Therapy for Achromatopsia
rAAV5-hCNGB3 Gene Therapy for Achromatopsia
|
|
06-2010
|
MY07A Gene Therapy for Usher 1B
MY07A Gene Therapy for Usher 1B
|
|
05-2010
|
AAV-RPE65 Gene Therapy Trial for LCA due to RPE65 Mutati
AAV-RPE65 Gene Therapy Trial for LCA due to RPE65 Mutati
|
|
05-2010
|
Usher 3A
Usher 3A
|
|
04-2010
|
Leber Hereditary Optic Neuropathy-Module 2 Year2
Leber Hereditary Optic Neuropathy-Module 2 Year2
|
|
04-2010
|
Leber Hereditary Optic Neuropathy:Gene Therapy Mod 3 Yr2
Leber Hereditary Optic Neuropathy:Gene Therapy Mod 3 Yr2
|
|
02-2010
|
Establishing channelrhodopsin as a tool to restore visua
Establishing channelrhodopsin as a tool to restore visua
|
|
12-2009
|
RESEARCH TRAINING IN VISION SCIENCE
RESEARCH TRAINING IN VISION SCIENCE
|
|
07-2009
|
Clinical Trials of Gene Therqapy for Leber Congenital Am
Clinical Trials of Gene Therqapy for Leber Congenital Am
|
|
06-2009
|
Novel Mechanisms and Therapies Targeting Dysfunctional
Novel Mechanisms and Therapies Targeting Dysfunctional
|
|
05-2009
|
PPG - Immunoregulatory Based Therapies for TYpe 1 Diabet
PPG - Immunoregulatory Based Therapies for TYpe 1 Diabet
|
|
04-2009
|
Leber Herditary Optic Neuropathy
Leber Herditary Optic Neuropathy
|
|
04-2009
|
Leber Hereditary Optic Neuropathy
Leber Hereditary Optic Neuropathy
|
|
01-2009
|
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
|
|
08-2008
|
Analysis of Subretinal AAV2-CBA-sFLT01 in the Laser CNV
Analysis of Subretinal AAV2-CBA-sFLT01 in the Laser CNV
|
|
08-2008
|
Modifcation of AdenoAssociated Virus to deliver DNA
Modifcation of AdenoAssociated Virus to deliver DNA
|
|
07-2008
|
Leber Hereditary Optic Neuropathy: Gene Therapy
Leber Hereditary Optic Neuropathy: Gene Therapy
|
|
06-2008
|
Cone Targeted Gene Therapy
Cone Targeted Gene Therapy
|
|
05-2008
|
Immunoregulatory Based Therapies for Type 1 Diabetes
Immunoregulatory Based Therapies for Type 1 Diabetes
|
|
05-2008
|
GENE THERAPY FOR CLARIN-MEDIATED USHERS 3A
GENE THERAPY FOR CLARIN-MEDIATED USHERS 3A
|
|
05-2008
|
Study of anit-neovascular genes for treatment of diabete
Study of anit-neovascular genes for treatment of diabete
|
|
10-2007
|
Functional Screening of Antineovascularization (NV) Gene
Functional Screening of Antineovascularization (NV) Gene
|
|
08-2007
|
LEBER HEREDITY OPTIC NEUROPATHY: GENE THERAPY
LEBER HEREDITY OPTIC NEUROPATHY: GENE THERAPY
|
|
07-2007
|
Gene Therapy for Leber Congenital Amaurosis
Gene Therapy for Leber Congenital Amaurosis
|
|
06-2007
|
Novel Mechanisms and Therapies Targeting Dysfunctional E
Novel Mechanisms and Therapies Targeting Dysfunctional E
|
|
05-2007
|
Functional Screening of Antineovascularization (NV) Gene
Functional Screening of Antineovascularization (NV) Gene
|
|
05-2007
|
Immunoregulatory Based Therapies for Type 1 Diabetes
Immunoregulatory Based Therapies for Type 1 Diabetes
|
|
04-2007
|
MODULATING THE FOLDING OF P23H OPSIN BY CHAPERONES
MODULATING THE FOLDING OF P23H OPSIN BY CHAPERONES
|
|
02-2007
|
FFB Board of Trustees Retinal Degeneration Research Awar
FFB Board of Trustees Retinal Degeneration Research Awar
|
|
07-2006
|
Gene Therapy for X-Linked Juvenile Retinoschisis
Gene Therapy for X-Linked Juvenile Retinoschisis
|
|
07-2006
|
GENE THERAPY FOR LEBER CONGENITAL AMAUROSIS
GENE THERAPY FOR LEBER CONGENITAL AMAUROSIS
|
|
06-2006
|
OPTIC NEURITIS: GENE THERAPY
OPTIC NEURITIS: GENE THERAPY
|
|
06-2006
|
TREATMENT OF AUTOSOMAL DOMINANT EYE DISEASE USING CATALY
TREATMENT OF AUTOSOMAL DOMINANT EYE DISEASE USING CATALY
|
|
06-2006
|
JDRF Gene Therapy Center
JDRF Gene Therapy Center
|
|
02-2006
|
DEVELOPING VIRAL VECTORS FOR GENE THERAPY OF CANINE MODE
DEVELOPING VIRAL VECTORS FOR GENE THERAPY OF CANINE MODE
|
|
01-2006
|
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
|
|
01-2006
|
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
|
|
01-2006
|
MOLECULAR BIOLOGY OF AAV: ANTI-NEOVASCULARIZATION THEORY
MOLECULAR BIOLOGY OF AAV: ANTI-NEOVASCULARIZATION THEORY
|
|
12-2005
|
MASSACHUSETTS GENERAL HOSPITAL
MASSACHUSETTS GENERAL HOSPITAL
|
|
09-2005
|
RESEARCH TRAINING IN VISION SCIENCE
RESEARCH TRAINING IN VISION SCIENCE
|
|
09-2005
|
Paul Kayser International Award in Retina Research
Paul Kayser International Award in Retina Research
|
|
07-2005
|
Gene Therapy for Leber Congenital Amaurosis
Gene Therapy for Leber Congenital Amaurosis
|
|
07-2005
|
GENE THERAPY FOR X-LINKED JUVENILE RETINOSCHISIS
GENE THERAPY FOR X-LINKED JUVENILE RETINOSCHISIS
|
|
07-2005
|
RETINAL GENE DELIVERY BY ADENO-ASSOCIATED VIRUS
RETINAL GENE DELIVERY BY ADENO-ASSOCIATED VIRUS
|
|
06-2005
|
GENE THERAPY FOR X-LINKED JUVENILE RETINOSCHISIS
GENE THERAPY FOR X-LINKED JUVENILE RETINOSCHISIS
|
|
06-2005
|
OPTIMIZING AAV-VECTORED GENE THERAPY FOR AMD-ASSOCIATED
OPTIMIZING AAV-VECTORED GENE THERAPY FOR AMD-ASSOCIATED
|
|
05-2005
|
FUNCTIONAL SCREENING OF ANTINEOVASCULARIZATION (NV) GENE
FUNCTIONAL SCREENING OF ANTINEOVASCULARIZATION (NV) GENE
|
|
12-2004
|
GENE THERAPY CENTER FOR THE PREVENTION OF DIABETES AND D
GENE THERAPY CENTER FOR THE PREVENTION OF DIABETES AND D
|
|
09-2004
|
RESEARCH TRAINING IN VISION SCIENCE
RESEARCH TRAINING IN VISION SCIENCE
|
|
09-2004
|
RESEARCH TRAINING IN VISION SCIENCE
RESEARCH TRAINING IN VISION SCIENCE
|
|
09-2004
|
RESEARCH TRAINING IN VISION SCIENCE
RESEARCH TRAINING IN VISION SCIENCE
|
|
05-2004
|
OPTIMIZING RIBOZYMES FOR TREATMENT OF INHERITED RETINAL
OPTIMIZING RIBOZYMES FOR TREATMENT OF INHERITED RETINAL
|
|
05-2004
|
RIBOZYNE THERAPY FOR AUTOSOMAL DOMINANT RETINITIS PIGMEN
RIBOZYNE THERAPY FOR AUTOSOMAL DOMINANT RETINITIS PIGMEN
|
|
12-2003
|
RESEARCH TO PREVENT BLINDNESS
RESEARCH TO PREVENT BLINDNESS
|
|
11-2003
|
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
ADENO-ASSOCIATED VIRUS MEDIATED GENE TRANSFER TO THE NER
|
|
08-2003
|
MOLECULAR BIOLOGY OF AAV: ANTI-NEOVASCULARIZATION THERAP
MOLECULAR BIOLOGY OF AAV: ANTI-NEOVASCULARIZATION THERAP
|
|
08-2003
|
LEBER HEREDITARY OPTIC NEUROPATHY: GENE THERAPY
LEBER HEREDITARY OPTIC NEUROPATHY: GENE THERAPY
|
|
08-2003
|
TOWARDS A PRIMATE MODEL and GENE THERAPY FOR MACULAR DISEA
TOWARDS A PRIMATE MODEL and GENE THERAPY FOR MACULAR DISEA
|
|
01-2003
|
RIBOZYME-MEDIATED IN VIVO PHOTORECPTOR EXPRESSION PROFIL
RIBOZYME-MEDIATED IN VIVO PHOTORECPTOR EXPRESSION PROFIL
|
|
03-2002
|
DELIVERY TECHNIQUES FOR RETINAL GENE EXPRESSION BY AAV
DELIVERY TECHNIQUES FOR RETINAL GENE EXPRESSION BY AAV
|
|
03-2002
|
MOLECULAR BIOLOGY OF AAV: ANTI-NEOVASCULARIZATION THERAP
MOLECULAR BIOLOGY OF AAV: ANTI-NEOVASCULARIZATION THERAP
|
|
09-2001
|
RESEARCH IN VISION SCIENCE
RESEARCH IN VISION SCIENCE
|
|
06-2001
|
TREATMENT OF AUTOSOMAL DOMINANT EYE DISEASE USING CATALY
TREATMENT OF AUTOSOMAL DOMINANT EYE DISEASE USING CATALY
|
|
05-2001
|
VIRAL MEDIATED RIBOZYME FOR RETINITIS PIGMENTOSA
VIRAL MEDIATED RIBOZYME FOR RETINITIS PIGMENTOSA
|
|
03-2001
|
PHOTORECEPTOR GENE EXPRESSION IN FETAL MAMMALIAN RETINA
PHOTORECEPTOR GENE EXPRESSION IN FETAL MAMMALIAN RETINA
|
|
05-2000
|
VIRAL MEDIATED RIBOZYME THERAPY FOR RETINITIS PIGMENTOSA
VIRAL MEDIATED RIBOZYME THERAPY FOR RETINITIS PIGMENTOSA
|
|
05-2000
|
GENE THERAPY FOR MITOCHONDRIAL DISEASE
GENE THERAPY FOR MITOCHONDRIAL DISEASE
|
|
09-1999
|
RESEARCH TRAINING IN VISION SCIENCE
RESEARCH TRAINING IN VISION SCIENCE
|
|
08-1999
|
RIBOZYME THERAPY FOR AUTOSOMAL DOMINANT RETINITIS PIGMEN
RIBOZYME THERAPY FOR AUTOSOMAL DOMINANT RETINITIS PIGMEN
|
|
06-1999
|
VIRAL MEDIATED RIBOZYME THERAPY FOR RETINITIS PIGMENTOSA
VIRAL MEDIATED RIBOZYME THERAPY FOR RETINITIS PIGMENTOSA
|
